Casgevy also now indicated for transfusion-dependent beta thalassemia in children 2 years ...

Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these ...

A handful of start-up firms are testing therapies that target specific epigenetic markers to treat everything from high ...

The company seems to be doing everything it's supposed to be doing; the stock just isn't responding.

The gene editing tool known as CRISPR-Cas9 is changing what's possible for treating a wide range of diseases caused by genetic mutations. But so far, attempts to use the technology to address ...

A handful of start-up firms are testing therapies that target specific epigenetic markers to treat everything from high ...

The inventor of the groundbreaking Crispr gene-editing technology is skeptical about artificial intelligence replacing human ...

Researchers discovered the secret checkpoints that keep CRISPR precise, revealing how the tool shifts from inactive to active without misfiring. The insight could transform gene therapy, making ...

A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based gene editing to treat a child with a rare genetic disorder. Unlike earlier ...

Emerging gene-editing platforms are demonstrating that disease-causing mutations, aberrant gene expression, and even large-scale DNA insertions can be corrected without relying on error-prone DNA ...